Miller TM, Cudkowicz ME, Shaw PJ, et al. Safety, PK, PD, and exploratory efficacy in single and multiple dose study of a SOD1 antisense oligonucleotide (BIIB067) administered to participants with ALS. AAN 2019, emerging science 007.
ECTRIMS 2015 video update Bouma: Parallel Session 2 New challenges in clinical trial design
jun 2017