Vichinsky E, Hoppe CC, Ataga KI, et al. Results from the randomized placebo-controlled phase 3 HOPE trial of voxelotor in adults and adolescents with sickle cell disease. 24th Congress of EHA, abstract S147.
Positief advies vergoeding etranacogene dezaparvovec (Hemgenix) voor behandeling hemofilie B
jul 2024 | Benigne hematologie